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Metadata
ID DOID:0050799
PURL http://purl.obolibrary.org/obo/DOID_0050799 Copy
Name guanidinoacetate methyltransferase deficiency
Definition A cerebral creatine deficiency syndrome that is characterized by severe intellectual disability, seizures, speech problems and involuntary movements, has_material_basis_in homozygous or compound heterozygous mutation in the GAMT gene on chromosome 19p13.
https://rarediseases.info.nih.gov/diseases/2578/guanidinoacetate-methyltransferase-deficiency
Xrefs

GARD:2578

MESH:C537622

MIM:612736

Subsets

DO_rare_slim

Synonyms

Cerebral creatine deficiency syndrome 2 [EXACT]

GAMT deficiency [EXACT]

Parent Relationships

is_a cerebral creatine deficiency syndrome

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